Prion Disease Treatment: Breakthroughs in Gene-Editing Therapy

April 7, 2025

Prion disease treatment is currently making strides that promise hope for patients afflicted by these devastating disorders, including conditions like Creutzfeldt-Jakob disease and fatal familial insomnia.Recent advancements in gene-editing therapy, particularly the innovative base editing technology, have demonstrated potential in targeting the prion protein gene responsible for these ailments.
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